FDA approves first gene-editing treatment for human illness
Dec 8, 2023 · The Food and Drug Administration approved two genetic treatments for sickle cell disease, including one that uses gene-editing. The approvals offer hope for patients and signal a new medical era.
What is CRISPR? A bioengineer explains | Stanford Report
The short answer: CRISPR is an immune system used by microbes to find and eliminate unwanted invaders. Qi: CRISPR stands for “clustered interspaced short palindromic repeats.” Biologists use ...
CRISPR Clinical Trials: A 2024 Update
March 13, 2024 Perspectives. By Hope Henderson. It is a remarkable time for the development of CRISPR -based therapies. In late 2023, we saw the first-ever approval of CRISPR-based medicine: Casgevy, a cure for sickle cell disease (SCD) and transfusion-dependent beta thalassemia (TDT).
The world's 1st CRISPR therapy has been approved. Here's …
Jan 18, 2024 · Drug regulators have approved a CRISPR therapy called Casgevy to treat inherited blood disorders. But what is it and how does it work?
FDA approves cure for sickle cell disease, the first ... - NBC News
Dec 8, 2023 · The therapy, called Casgevy, from Vertex Pharmaceuticals and CRISPR Therapeutics, is the first medicine to be approved in the United States that uses the gene-editing tool CRISPR, which won its...
CRISPR 2.0: a new wave of gene editors heads for clinical trials
Dec 7, 2023 · Less than a month after the world’s first approval of a CRISPR–Cas9 genome-editing therapy, researchers are hoping that the therapy will win its second authorization this week — this time...
‘ChatGPT for CRISPR’ creates new gene-editing tools - Nature
Apr 29, 2024 · This week, researchers published details of how they used a generative AI tool called a protein language model — a neural network trained on millions of protein sequences — to design CRISPR...
FDA Approves First CRISPR Treatment in U.S. | TIME
Dec 8, 2023 · CRISPR can increase the population of healthy blood cells in both groups of patients. The FDA approved exa-cel for sickle cell disease, and will make a decision about treating beta thalassemia by...
The world’s first CRISPR therapy is approved: who will ... - Nature
Nov 21, 2023 · The UK’s regulator has approved the world’s first CRISPR–Cas9 gene editing therapy, which aims to cure sickle cell disease and transfusion-dependent β-thalassemia.
Search algorithm reveals nearly 200 new kinds of CRISPR systems
Nov 23, 2023 · A new search algorithm has identified 188 kinds of new CRISPR systems in bacterial genomes. The systems have a range of functions and could enable gene editing, diagnostics, and more.